chapter 99 — references - health library self serve/ppo10e... · r338 chapter 99 references 62....

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1. Howlader N, Noone AM, Krapcho M, et al., eds. SEER Cancer Statistics Review, 1975-2010. Bethesda, MD: National Cancer Institute; 2013. 2. Smith MA, Seibel NL, Altekruse SF, et al. Outcomes for children and ado- lescents with cancer: challenges for the twenty-first century. J Clin Oncol 2010;28:2625–2634. 3. Janeway KA, Place AE, Kieran MW, et al. Future of clinical genomics in pediatric oncology. J Clin Oncol 2013;31:1893–1903. 4. Berg SL, Grisell DL, DeLaney TF, et al. Principles of treatment of pediatric solid tumors. Pediatr Clin North Am 1991;38:249–267. 5. Meyers PA, Schwartz CL, Krailo M, et al. Osteosarcoma: a randomized, pro- spective trial of the addition of ifosfamide and/or muramyl tripeptide to cisplat- in, doxorubicin, and high-dose methotrexate. J Clin Oncol 2005;23:2004–2011. 6. Blakely ML, Lobe TE, Anderson JR, et al. Does debulking improve sur- vival rate in advanced-stage retroperitoneal embryonal rhabdomyosarcoma? Pediatr Surg 1999;34:736–741. 7. Simon T, Haberle B, Hero B, et al. Role of surgery in the treatment of pa- tients with stage 4 neuroblastoma age 18 months or older at diagnosis. J Clin Oncol 2013;31:752–758. 8. Raney B, Stoner J, Anderson J, et al. Impact of tumor viability at second-look procedures performed before completing treatment on the Intergroup Rhab- domyosarcoma Study Group protocol IRS-IV, 1991-1997: a report from the children’s oncology group. J Pediatr Surg 2010;45:2160–2168. 9. Flamant F, Rodary C, Rey A, et al. Treatment of non-metastatic rhabdo- myosarcomas in childhood and adolescence. Results of the second study of the International Society of Paediatric Oncology: MMT84. Eur J Cancer 1998;34:1050–1062. 10. Crist W, Gehan EA, Ragab AH, et al. The Third Intergroup Rhabdomyosar- coma Study. J Clin Oncol 1995;13:610–630. 11. Brodeur GM. Neuroblastoma: biological insights into a clinical enigma. Nat Rev Cancer 2003;3:203–216. 12. Maris JM, Hogarty MD, Bagatell R, et al. Neuroblastoma. Lancet 2007; 369:2106–2120. 13. Maris JM. Recent advances in neuroblastoma. N Engl J Med 2010;362: 2202–2211. 14. Park JR, Eggert A, Caron H. Neuroblastoma: biology, prognosis, and treat- ment. Hematol Oncol Clin North Am 2010;24:65–86. 15. Maris JM. The biologic basis for neuroblastoma heterogeneity and risk strati- fication. Curr Opin Pediatr 2005;17:7–13. 16. Goodman MT, Gurney JG, Smith MA, et al. Sympathetic nervous system tumors. In: Ries LAG, Smith MA, Gurney JG, et al., eds. Cancer Incidence and Survival among Children and Adolescents: United States SEER Program 1975-1995. National Cancer Institute, SEER Program. Bethesda, MD: Na- tional Cancer Institute; 1999: 65–72. 17. London WB, Castleberry RP, Matthay KK, et al. Evidence for an age cut- off greater than 365 days for neuroblastoma risk group stratification in the Children’s Oncology Group. J Clin Oncol 2005;23:6459–6465. 18. Kushner BH, Gilbert F, Helson L. Familial neuroblastoma. Case reports, literature review, and etiologic considerations. Cancer 1986;57:1887–1893. 19. Maris JM, Kyemba SM, Rebbeck TR, et al. Molecular genetic analysis of familial neuroblastoma. Eur J Cancer 1997;33:1923–1928. 20. Maris JM, Weiss MJ, Mosse Y, et al. Evidence for a hereditary neuroblastoma predisposition locus at chromosome 16p12-13. Cancer Res 2002;62:6651–6658. 21. Tonini GP, Longo L, Coco S, et al. Familial neuroblastoma: a complex heri- table disease. Cancer Lett 2003;197:41–45. 22. Shojaei-Brosseau T, Chompret A, Abel A, et al. Genetic epidemiology of neuroblastoma: a study of 426 cases at the Institut Gustave-Roussy in France. Pediatr Blood Cancer 2004;42:99–105. 23. Longo L, Panza E, Schena F, et al. Genetic predisposition to familial neuro- blastoma: identification of two novel genomic regions at 2p and 12p. Human Hered 2007;63:205–211. 24. Knudson AG Jr, Strong LC. Mutation and cancer: neuroblastoma and pheo- chromocytoma. Am J Hum Genet 1972;24:514–532. 25. Mosse YP, Laudenslager M, Longo L, et al. Identification of ALK as a major familial neuroblastoma predisposition gene. Nature 2008;455:930–935. 26. Lemire EG, Chodirker BN, Williams GJ, et al. Familial neuroblastoma: re- port of a kindred with later age at diagnosis. J Pediatr Hematol Oncol 1998; 20:489–493. 27. Chen Y, Takita J, Choi YL, et al. Oncogenic mutations of ALK kinase in neuroblastoma. Nature 2008;455:971–974. 28. George RE, Sanda T, Hanna M, et al. Activating mutations in ALK provide a therapeutic target in neuroblastoma. Nature 2008;455:975–978. 29. Janoueix-Lerosey I, Lequin D, Brugieres L, et al. Somatic and germline activating mutations of the ALK kinase receptor in neuroblastoma. Nature 2008;455:967–970. 30. Ogawa S, Takita J, Sanada M, et al. Oncogenic mutations of ALK in neuro- blastoma. Cancer Sci 2011;102:302–308. 31. Trochet D, Bourdeaut F, Janoueix-Lerosey I, et al. Germline mutations of the paired-like homeobox 2B (PHOX2B) gene in neuroblastoma. Am J Hum Genet 2004;74:761–764. 32. Mosse YP, Laundenslager M, Khazi D, et al. Germline PHOX2B mutation in hereditary neuroblastoma. Am J Hum Genet 2004;75:727–730. 33. Raabe EH, Laundeslager M, Winter C, et al. Prevalence and functional consequence of PHOX2B mutations in neuroblastoma. Oncogene 2008;27: 469–476. 34. Nemecek ER, Sawin RW, Park J. Treatment of neuroblastoma in patients with neurocristopathy syndromes. J Pediatr Hematol Oncol 2003;25:159–162. 35. Maris JM, Chatten J, Meadows AT, et al. Familial neuroblastoma: a three- generation pedigree and a further association with Hirschsprung disease. Med Pediatr Oncol 1997;28:1–5. 36. Stovroff M, Dykes F, Teague WG. The complete spectrum of neurocristopa- thy in an infant with congenital hypoventilation, Hirschsprung’s disease, and neuroblastoma. J Pediatr Surg 1995;30:1218–1221. 37. Kushner BH, Hajdu SI, Helson L. Synchronous neuroblastoma and von Recklinghausen’s disease: a review of the literature. J Clin Oncol 1985;3: 117–120. 38. The I, Murthy AE, Hannigan GE, et al. Neurofibromatosis type 1 gene muta- tions in neuroblastoma. Nat Genet 1993;3:62–66. 39. Blatt J, Olshan AF, Lee PA, Ross JL. Neuroblastoma and related tumors in Turner’s syndrome. J Pediatr 1997;131:666–670. 40. DeBaun MR, Tucker MA. Risk of cancer during the first four years of life in children from The Beckwith-Wiedemann Syndrome Registry. J Pediatr 1998;132:398–400. 41. Anderson DJ, Carnahan JF, Michelsohn A, et al. Antibody markers identify a common progenitor to sympathetic neurons and chromaffin cells in vivo and reveal the timing of commitment to neuronal differentiation in the sympa- thoadrenal lineage. J Neurosci 1991;11:3507–3519. 42. Shimada H, Chatten J, Newton WA Jr, et al. Histopathologic prognostic factors in neuroblastic tumors: definition of subtypes of ganglioneuroblas- toma and an age-linked classification of neuroblastomas. J Natl Cancer Inst 1984;73:405–416. 43. Shimada H, Ambros IM, Dehner LP, et al. Terminology and morphologic criteria of neuroblastic tumors: recommendations by the International Neu- roblastoma Pathology Committee. Cancer 1999;86:349–363. 44. Shimada H, Ambros IM, Dehner LP, et al. The International Neuro- blastoma Pathology Classification (the Shimada system). Cancer 1999;86: 364–372. 45. Peuchmaur M, d’Amore ES, Joshi VV, et al. Revision of the International Neuroblastoma Pathology Classification: confirmation of favorable and unfavorable prognostic subsets in ganglioneuroblastoma, nodular. Cancer 2003;98:2274–2281. 46. Shimada H, Umehara S, Monobe Y, et al. International neuroblastoma pa- thology classification for prognostic evaluation of patients with peripheral neuroblastic tumors: a report from the Children’s Cancer Group. Cancer 2001;92:2451–2461. 47. Schwab M, Alitalo K, Klempnauer KH, et al. Amplified DNA with limited homology to myc cellular oncogene is shared by human neuroblastoma cell lines and a neuroblastoma tumour. Nature 1983;305:245–248. 48. Brodeur GM, Seeger RC, Schwab M, et al. Amplification of N-myc in untreated human neuroblastomas correlates with advanced disease stage. Science 1984;224:1121–1124. 49. Seeger RC, Brodeur GM, Sather H, et al. Association of multiple copies of the N-myc oncogene with rapid progression of neuroblastomas. N Engl J Med 1985;313:1111–1116. 50. Maris JM, Matthay KK. Molecular biology of neuroblastoma. J Clin Oncol 1999;17:2264–2279. 51. Cohn SL, Pearson AD, London WB, et al. The International Neuroblastoma Risk Group (INRG) classification system: an INRG Task Force report. J Clin Oncol 2009;27:289–297. 52. Kaneko Y, Kanda N, Maseki N, et al. Different karyotypic patterns in early and advanced stage neuroblastomas. Cancer Res 1987;47:311–318. 53. Look AT, Hayes FA, Nitschke R, et al. Cellular DNA content as a predictor of response to chemotherapy in infants with unresectable neuroblastoma. N Engl J Med 1984;311:231–235. 54. Look AT, Hayes FA, Shuster JJ, et al. Clinical relevance of tumor cell ploidy and N-myc gene amplification in childhood neuroblastoma: a Pediatric Oncology Group study. J Clin Oncol 1991;9:581–591. 55. Attiyeh EF, London WB, Mosse YP, et al. Chromosome 1p and 11q deletions and outcome in neuroblastoma. N Engl J Med 2005;353:2243–2253. 56. Bown N, Cotterill S, Lastowska M, et al. Gain of chromosome arm 17q and adverse outcome in patients with neuroblastoma. N Engl J Med 1999;340: 1954–1961. 57. Brodeur GM, et al. Trk receptor expression and inhibition in neuroblasto- mas. Clin Cancer Res 2009;15:3244–3250. 58. Ho R, Eggert A, Hishiki T, et al. Resistance to chemotherapy mediated by TrkB in neuroblastomas. Cancer Res 2002;62:6462–6466. 59. Cheung NK, Zhang J, Lu C, et al. Association of age at diagnosis and genetic mutations in patients with neuroblastoma. JAMA 2012;307:1062–1071. 60. Vandepoele K, Van Roy N, Staes K, et al. A novel gene family NBPF: intri- cate structure generated by gene duplications during primate evolution. Mol Biol Evol 2005;22:2265–2274. 61. Diskin SJ, Hou C, Glessner JT, et al. Copy number variation at 1q21.1 associ- ated with neuroblastoma. Nature 2009;459:987–991. CHAPTER 99 — REFERENCES Devita_References.indd 337 10/23/14 4:22 AM

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Page 1: CHAPTER 99 — REFERENCES - Health Library Self Serve/PPO10e... · R338 Chapter 99 References 62. Janoueix-Lerosey I, Schleiermacher G, Michels E, et al. Overall genomic pattern is

1. Howlader N, Noone AM, Krapcho M, et al., eds. SEER Cancer Statistics Review, 1975-2010. Bethesda, MD: National Cancer Institute; 2013.

2. Smith MA, Seibel NL, Altekruse SF, et al. Outcomes for children and ado-lescents with cancer: challenges for the twenty-first century. J Clin Oncol 2010;28:2625–2634.

3. Janeway KA, Place AE, Kieran MW, et al. Future of clinical genomics in pediatric oncology. J Clin Oncol 2013;31:1893–1903.

4. Berg SL, Grisell DL, DeLaney TF, et al. Principles of treatment of pediatric solid tumors. Pediatr Clin North Am 1991;38:249–267.

5. Meyers PA, Schwartz CL, Krailo M, et al. Osteosarcoma: a randomized, pro-spective trial of the addition of ifosfamide and/or muramyl tripeptide to cisplat-in, doxorubicin, and high-dose methotrexate. J Clin Oncol 2005;23:2004–2011.

6. Blakely ML, Lobe TE, Anderson JR, et al. Does debulking improve sur-vival rate in advanced-stage retroperitoneal embryonal rhabdomyosarcoma? J  Pediatr Surg 1999;34:736–741.

7. Simon T, Haberle B, Hero B, et al. Role of surgery in the treatment of pa-tients with stage 4 neuroblastoma age 18 months or older at diagnosis. J Clin Oncol 2013;31:752–758.

8. Raney B, Stoner J, Anderson J, et al. Impact of tumor viability at second-look procedures performed before completing treatment on the Intergroup Rhab-domyosarcoma Study Group protocol IRS-IV, 1991-1997: a report from the children’s oncology group. J Pediatr Surg 2010;45:2160–2168.

9. Flamant F, Rodary C, Rey A, et al. Treatment of non-metastatic rhabdo-myosarcomas in childhood and adolescence. Results of the second study of the International Society of Paediatric Oncology: MMT84. Eur J Cancer 1998;34:1050–1062.

10. Crist W, Gehan EA, Ragab AH, et al. The Third Intergroup Rhabdomyosar-coma Study. J Clin Oncol 1995;13:610–630.

11. Brodeur GM. Neuroblastoma: biological insights into a clinical enigma. Nat Rev Cancer 2003;3:203–216.

12. Maris JM, Hogarty MD, Bagatell R, et al. Neuroblastoma. Lancet 2007; 369:2106–2120.

13. Maris JM. Recent advances in neuroblastoma. N Engl J Med 2010;362: 2202–2211.

14. Park JR, Eggert A, Caron H. Neuroblastoma: biology, prognosis, and treat-ment. Hematol Oncol Clin North Am 2010;24:65–86.

15. Maris JM. The biologic basis for neuroblastoma heterogeneity and risk strati-fication. Curr Opin Pediatr 2005;17:7–13.

16. Goodman MT, Gurney JG, Smith MA, et al. Sympathetic nervous system tumors. In: Ries LAG, Smith MA, Gurney JG, et al., eds. Cancer Incidence and Survival among Children and Adolescents: United States SEER Program 1975-1995. National Cancer Institute, SEER Program. Bethesda, MD: Na-tional Cancer Institute; 1999: 65–72.

17. London WB, Castleberry RP, Matthay KK, et al. Evidence for an age cut-off greater than 365 days for neuroblastoma risk group stratification in the Children’s Oncology Group. J Clin Oncol 2005;23:6459–6465.

18. Kushner BH, Gilbert F, Helson L. Familial neuroblastoma. Case reports, literature review, and etiologic considerations. Cancer 1986;57:1887–1893.

19. Maris JM, Kyemba SM, Rebbeck TR, et al. Molecular genetic analysis of familial neuroblastoma. Eur J Cancer 1997;33:1923–1928.

20. Maris JM, Weiss MJ, Mosse Y, et al. Evidence for a hereditary neuroblastoma predisposition locus at chromosome 16p12-13. Cancer Res 2002;62:6651–6658.

21. Tonini GP, Longo L, Coco S, et al. Familial neuroblastoma: a complex heri-table disease. Cancer Lett 2003;197:41–45.

22. Shojaei-Brosseau T, Chompret A, Abel A, et al. Genetic epidemiology of neuroblastoma: a study of 426 cases at the Institut Gustave-Roussy in France. Pediatr Blood Cancer 2004;42:99–105.

23. Longo L, Panza E, Schena F, et al. Genetic predisposition to familial neuro-blastoma: identification of two novel genomic regions at 2p and 12p. Human Hered 2007;63:205–211.

24. Knudson AG Jr, Strong LC. Mutation and cancer: neuroblastoma and pheo-chromocytoma. Am J Hum Genet 1972;24:514–532.

25. Mosse YP, Laudenslager M, Longo L, et al. Identification of ALK as a major familial neuroblastoma predisposition gene. Nature 2008;455:930–935.

26. Lemire EG, Chodirker BN, Williams GJ, et al. Familial neuroblastoma: re-port of a kindred with later age at diagnosis. J Pediatr Hematol Oncol 1998; 20:489–493.

27. Chen Y, Takita J, Choi YL, et al. Oncogenic mutations of ALK kinase in neuroblastoma. Nature 2008;455:971–974.

28. George RE, Sanda T, Hanna M, et al. Activating mutations in ALK provide a therapeutic target in neuroblastoma. Nature 2008;455:975–978.

29. Janoueix-Lerosey I, Lequin D, Brugieres L, et al. Somatic and germline activating mutations of the ALK kinase receptor in neuroblastoma. Nature 2008;455:967–970.

30. Ogawa S, Takita J, Sanada M, et al. Oncogenic mutations of ALK in neuro-blastoma. Cancer Sci 2011;102:302–308.

31. Trochet D, Bourdeaut F, Janoueix-Lerosey I, et al. Germline mutations of the paired-like homeobox 2B (PHOX2B) gene in neuroblastoma. Am J Hum Genet 2004;74:761–764.

32. Mosse YP, Laundenslager M, Khazi D, et al. Germline PHOX2B mutation in hereditary neuroblastoma. Am J Hum Genet 2004;75:727–730.

33. Raabe EH, Laundeslager M, Winter C, et al. Prevalence and functional consequence of PHOX2B mutations in neuroblastoma. Oncogene 2008;27: 469–476.

34. Nemecek ER, Sawin RW, Park J. Treatment of neuroblastoma in patients with neurocristopathy syndromes. J Pediatr Hematol Oncol 2003;25:159–162.

35. Maris JM, Chatten J, Meadows AT, et al. Familial neuroblastoma: a three-generation pedigree and a further association with Hirschsprung disease. Med Pediatr Oncol 1997;28:1–5.

36. Stovroff M, Dykes F, Teague WG. The complete spectrum of neurocristopa-thy in an infant with congenital hypoventilation, Hirschsprung’s disease, and neuroblastoma. J Pediatr Surg 1995;30:1218–1221.

37. Kushner BH, Hajdu SI, Helson L. Synchronous neuroblastoma and von Recklinghausen’s disease: a review of the literature. J Clin Oncol 1985;3: 117–120.

38. The I, Murthy AE, Hannigan GE, et al. Neurofibromatosis type 1 gene muta-tions in neuroblastoma. Nat Genet 1993;3:62–66.

39. Blatt J, Olshan AF, Lee PA, Ross JL. Neuroblastoma and related tumors in Turner’s syndrome. J Pediatr 1997;131:666–670.

40. DeBaun MR, Tucker MA. Risk of cancer during the first four years of life in children from The Beckwith-Wiedemann Syndrome Registry. J Pediatr 1998;132:398–400.

41. Anderson DJ, Carnahan JF, Michelsohn A, et al. Antibody markers identify a common progenitor to sympathetic neurons and chromaffin cells in vivo and reveal the timing of commitment to neuronal differentiation in the sympa-thoadrenal lineage. J Neurosci 1991;11:3507–3519.

42. Shimada H, Chatten J, Newton WA Jr, et al. Histopathologic prognostic factors in neuroblastic tumors: definition of subtypes of ganglioneuroblas-toma and an age-linked classification of neuroblastomas. J Natl Cancer Inst 1984;73:405–416.

43. Shimada H, Ambros IM, Dehner LP, et al. Terminology and morphologic criteria of neuroblastic tumors: recommendations by the International Neu-roblastoma Pathology Committee. Cancer 1999;86:349–363.

44. Shimada H, Ambros IM, Dehner LP, et al. The International Neuro-blastoma Pathology Classification (the Shimada system). Cancer 1999;86: 364–372.

45. Peuchmaur M, d’Amore ES, Joshi VV, et al. Revision of the International Neuroblastoma Pathology Classification: confirmation of favorable and unfavorable prognostic subsets in ganglioneuroblastoma, nodular. Cancer 2003;98:2274–2281.

46. Shimada H, Umehara S, Monobe Y, et al. International neuroblastoma pa-thology classification for prognostic evaluation of patients with peripheral neuroblastic tumors: a report from the Children’s Cancer Group. Cancer 2001;92:2451–2461.

47. Schwab M, Alitalo K, Klempnauer KH, et al. Amplified DNA with limited homology to myc cellular oncogene is shared by human neuroblastoma cell lines and a neuroblastoma tumour. Nature 1983;305:245–248.

48. Brodeur GM, Seeger RC, Schwab M, et al. Amplification of N-myc in untreated human neuroblastomas correlates with advanced disease stage. Science 1984;224:1121–1124.

49. Seeger RC, Brodeur GM, Sather H, et al. Association of multiple copies of the N-myc oncogene with rapid progression of neuroblastomas. N Engl J Med 1985;313:1111–1116.

50. Maris JM, Matthay KK. Molecular biology of neuroblastoma. J Clin Oncol 1999;17:2264–2279.

51. Cohn SL, Pearson AD, London WB, et al. The International Neuroblastoma Risk Group (INRG) classification system: an INRG Task Force report. J Clin Oncol 2009;27:289–297.

52. Kaneko Y, Kanda N, Maseki N, et al. Different karyotypic patterns in early and advanced stage neuroblastomas. Cancer Res 1987;47:311–318.

53. Look AT, Hayes FA, Nitschke R, et al. Cellular DNA content as a predictor of response to chemotherapy in infants with unresectable neuroblastoma. N Engl J Med 1984;311:231–235.

54. Look AT, Hayes FA, Shuster JJ, et al. Clinical relevance of tumor cell ploidy and N-myc gene amplification in childhood neuroblastoma: a Pediatric Oncology Group study. J Clin Oncol 1991;9:581–591.

55. Attiyeh EF, London WB, Mosse YP, et al. Chromosome 1p and 11q deletions and outcome in neuroblastoma. N Engl J Med 2005;353:2243–2253.

56. Bown N, Cotterill S, Lastowska M, et al. Gain of chromosome arm 17q and adverse outcome in patients with neuroblastoma. N Engl J Med 1999;340: 1954–1961.

57. Brodeur GM, et al. Trk receptor expression and inhibition in neuroblasto-mas. Clin Cancer Res 2009;15:3244–3250.

58. Ho R, Eggert A, Hishiki T, et al. Resistance to chemotherapy mediated by TrkB in neuroblastomas. Cancer Res 2002;62:6462–6466.

59. Cheung NK, Zhang J, Lu C, et al. Association of age at diagnosis and genetic mutations in patients with neuroblastoma. JAMA 2012;307:1062–1071.

60. Vandepoele K, Van Roy N, Staes K, et al. A novel gene family NBPF: intri-cate structure generated by gene duplications during primate evolution. Mol Biol Evol 2005;22:2265–2274.

61. Diskin SJ, Hou C, Glessner JT, et al. Copy number variation at 1q21.1 associ-ated with neuroblastoma. Nature 2009;459:987–991.

C H A P T E R 9 9 — R E F E R E N C E S

Devita_References.indd 337 10/23/14 4:22 AM

Page 2: CHAPTER 99 — REFERENCES - Health Library Self Serve/PPO10e... · R338 Chapter 99 References 62. Janoueix-Lerosey I, Schleiermacher G, Michels E, et al. Overall genomic pattern is

R338 Chapter 99 References

62. Janoueix-Lerosey I, Schleiermacher G, Michels E, et al. Overall genomic pattern is a predictor of outcome in neuroblastoma. J Clin Oncol 2009;27: 1026–1033.

63. De Preter K, Vermeulen J, Brors B, et al. Accurate outcome prediction in neuroblastoma across independent data sets using a multigene signature. Clin Cancer Res 2010;16:532–1541.

64. Schleiermacher G, Michon J, Huon I, et al. Chromosomal CGH identifies patients with a higher risk of relapse in neuroblastoma without MYCN am-plification. Br J Cancer 2007;97:238–246.

65. Mosse YP, Diskin SJ, Wasserman N, et al. Neuroblastomas have distinct ge-nomic DNA profiles that predict clinical phenotype and regional gene ex-pression. Genes Chromosomes Cancer 2007;46:936–949.

66. Oberthuer A, Berthold F, Warnat P, et al. Customized oligonucleotide micro-array gene expression-based classification of neuroblastoma patients outper-forms current clinical risk stratification. J Clin Oncol 2006;24:5070–5078.

67. Oberthuer A, Warnat P, Kahlert Y, et al. Classification of neuroblastoma patients by published gene-expression markers reveals a low sensitivity for unfavorable courses of MYCN non-amplified disease. Cancer Lett 2007;250: 250–267.

68. Tomioka N, Oba S, Ohira M, et al. Novel risk stratification of patients with neuroblastoma by genomic signature, which is independent of molecular signature. Oncogene 2008;27:441–449.

69. Maris JM, Mosse YP, Bradfield JP, et al. Chromosome 6p22 locus associ-ated with clinically aggressive neuroblastoma. N Engl J Med 2008;358: 2585–2593.

70. Capasso M, Devoto M, Hou C, et al. Common variations in BARD1 influ-ence susceptibility to high-risk neuroblastoma. Nat Genet 2009;41:718–723.

71. Wang K, Diskin SJ, Zhang H, et al. Integrative genomics identifies LMO1 as a neuroblastoma oncogene. Nature 2011;469:216–220.

72. DuBois SG, Kalika Y, Lukens JN, et al. Metastatic sites in stage IV and IVS neuroblastoma correlate with age, tumor biology, and survival. J Pediatr He-matol Oncol 1999;21:181–189.

73. Timmerman, R. Images in clinical medicine. Raccoon eyes and neuroblas-toma. N Engl J Med 2003;349:e4.

74. Simon T, Niemann CA, Hero B, et al. Short- and long-term outcome of patients with symptoms of spinal cord compression by neuroblastoma. Dev Med Child Neurol 2012;54:347–352.

75. Belgaumi AF, Kauffman WM, Jenkins JJ, et al. Blindness in children with neuroblastoma. Cancer 1997;80:1997–2004.

76. Lucky AW, McGuire J, Komp DM. Infantile neuroblastoma presenting with cutaneous blanching nodules. J Am Acad Dermatol 1982;6:389–391.

77. LaBrosse EH, Comoy E, Bohuon C, et al. Catecholamine metabolism in neuroblastoma. J Natl Cancer Inst 1976;57:633–638.

78. Monsaingeon M, Perel Y, Simonnet G, et al. Comparative values of cate-cholamines and metabolites for the diagnosis of neuroblastoma. Eur J Pediatr 2003;162:397–402.

79. Strenger V, Perel Y, Simonnet G, et al. Diagnostic and prognostic impact of urinary catecholamines in neuroblastoma patients. Pediatr Blood Cancer 2007;48:504–509.

80. O’Meara A, Tormey W, FitzGerald RJ, et al. Interpretation of random uri-nary catecholamines and their metabolites in neuroblastoma. Acta Paediatr 1994;83:88–92.

81. Bourdeaut F, de Carli E, Timsit S, et al. VIP hypersecretion as primary or secondary syndrome in neuroblastoma: A retrospective study by the Societe Francaise des Cancers de l’Enfant (SFCE). Pediatr Blood Cancer 2009;52:585–590.

82. Wilson J. Neuroimmunology of dancing eye syndrome in children. Dev Med Child Neurol 2006;48:693–696.

83. Gorman MP. Update on diagnosis, treatment, and prognosis in opsoclonus-myoclonus-ataxia syndrome. Curr Opin Pediatr 2010;22:745–750.

84. Brunklaus A, Pohl K, Zuberi SM, et al. Outcome and prognostic features in opsoclonus-myoclonus syndrome from infancy to adult life. Pediatrics 2011;128:e388–e394.

85. Raffaghello L, Conte M, De Grandis E, et al. Immunological mechanisms in opsoclonus-myoclonus associated neuroblastoma. Eur J Paediatr Neurol 2009;13:219–223.

86. Rudnick E, Khakoo Y, Antunes NL, et al. Opsoclonus-myoclonus-ataxia syn-drome in neuroblastoma: clinical outcome and antineuronal antibodies—a report from the Children’s Cancer Group Study. Med Pediatr Oncol 2001;36:612–622.

87. Matthay KK, Blaes F, Hero B, et al. Opsoclonus myoclonus syndrome in neuroblastoma a report from a workshop on the dancing eyes syndrome at the advances in neuroblastoma meeting in Genoa, Italy, 2004. Cancer Lett 2005;228:275–282.

88. Russo C, Cohn SL, Petruzzi MJ, et al. Long-term neurologic outcome in children with opsoclonus-myoclonus associated with neuroblastoma: a report from the Pediatric Oncology Group. Med Pediatr Oncol 1997;28:284–288.

89. Hayward K, Jeremy RJ, Jenkins S, et al. Long-term neurobehavioral outcomes in children with neuroblastoma and opsoclonus-myoclonus-ataxia syndrome: relationship to MRI findings and anti-neuronal antibodies. J Pedi-atr 2001;139:552–559.

90. De Bernardi B, Balwierz W, Bejent J, et al. Epidural compression in neu-roblastoma: Diagnostic and therapeutic aspects. Cancer Lett 2005;228: 283–299.

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